Medcare Women & Children Hospital has successfully administered a pioneering intrathecal gene therapy for Spinal Muscular Atrophy (SMA) to Hulus, a three-year-old patient from Turkey. This milestone ...
Significant unmet needs in SMA management include therapy access, fatigue, reproductive health, and emerging phenotypes in older patients. Intrathecal gene therapy offers potential for older SMA ...
“Trying to Be a Good Parent” As Defined By Interviews With Parents Who Made Phase I, Terminal Care, and Resuscitation Decisions for Their Children In this multisite study, 171 children with ...
Of a total of 156 patients, 152 were eligible. Seventeen patients did not have PB blasts at diagnosis. Three fourths of the remaining patients achieved complete clearance of PB blasts by d10. Only ...
PRIALT ® (ziconotide) is the only FDA-approved, non-opioid intrathecal infusion treatment option for patients suffering from severe chronic pain for whom intrathecal therapy is warranted, and who are ...
Gene therapy delivered for the first time via lumbar puncture showed promise of benefit in slowing progression of giant axonal neuropathy (GAN) in a phase I clinical trial. The slope of change in ...
Spanish privately-held pharma company entered into an agreement to acquire USA-based TerSera's Infusion Specialty Therapies ...
Boothwyn, PA., Jan. 08, 2026 (GLOBE NEWSWIRE) -- Pentec Health, Inc. (Pentec) today announced the acquisition of Hartley Medical Center Pharmacy, LLC (Hartley Medical), a nationally recognized ...
DUBAI, United Arab Emirates — Medcare Women & Children Hospital has successfully administered a pioneering intrathecal gene therapy for Spinal Muscular Atrophy (SMA) to Hulus, a three-year-old patient ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results